기본 정보
연구 분야
프로젝트
발행물
구성원
article|
gold
·인용수 3
·2025
Exploring gene-phenotype relationships in GRIN-related neurodevelopmental disorders
Jong‐Ho Cha, Jee Min Kim, Hee‐Jeong Yun, H.-J. Genie Chin, Hye Jin Kim, Woo Joong Kim, Soo Yeon Kim, Byung Chan Lim, Ki Joong Kim, Seungbok Lee, Jong‐Hee Chae
IF 4.8npj Genomic Medicine
초록

The GRIN family is implicated in neurological disorders, such as global developmental delay (GDD) and epilepsy. We reviewed 31 patients with GRIN-related neurodevelopmental disorders at Seoul National University Hospital; all exhibited profound GDD, with 58.1% unable to walk independently and 74.2% unable to speak meaningful words. In a pooled analysis with the GRIN portal data ( https://grin-portal.broadinstitute.org/ ), patients with missense or in-frame variants had significantly higher rates of profound GDD (74.3% vs. 30.4%, p < 0.001) and movement disorders (69.0% vs. 41.4%, p < 0.01) than those with protein-truncating variants. Furthermore, missense or in-frame variants in the M3 and M4 helices of the transmembrane domain were significantly associated with profound GDD (M3 helix: adjusted odds ratio [aOR] 8.48; 95% confidence interval [CI] 2.79-25.76; M4 helix: aOR 3.14; 95% CI 1.39-7.09) compared to those in other domains. Our findings highlight the importance of detailed variant characterization to inform personalized treatment strategies.

키워드
PhenotypeGeneGeneticsBiology
타입
article
IF / 인용수
4.8 / 3
게재 연도
2025